Assessment of primary outcome measures for a clinical trial of pediatric hemorrhagic injuries
Document Type
Journal Article
Publication Date
1-1-2020
Journal
American Journal of Emergency Medicine
DOI
10.1016/j.ajem.2020.03.001
Keywords
Children; Consensus; Outcome measure; Pediatric Quality of Life; Tranexamic acid; Trauma
Abstract
© 2020 Elsevier Inc. Objective: We evaluated the acceptability of the Pediatric Quality of Life Inventory (PedsQL) and other outcomes as the primary outcomes for a pediatric hemorrhagic trauma trial (TIC-TOC) among clinicians. Methods: We conducted a mixed-methods study that included an electronic questionnaire followed by teleconference discussions. Participants confirmed or rejected the PedsQL as the primary outcome for the TIC-TOC trial and evaluated and proposed alternative primary outcomes. Responses were compiled and a list of themes and representative quotes was generated. Results: 73 of 91 (80%) participants completed the questionnaire. 61 (84%) participants agreed that the PedsQL is an appropriate primary outcome for children with hemorrhagic brain injuries. 32 (44%) participants agreed that the PedsQL is an acceptable primary outcome for children with hemorrhagic torso injuries, 27 (38%) participants were neutral, and 13 (18%) participants disagreed. Several themes were identified from responses, including that the PedsQL is an important and patient-centered outcome but may be affected by other factors, and that intracranial hemorrhage progression assessed by brain imaging (among patients with brain injuries) or blood product transfusion requirements (among patients with torso injuries) may be more objective outcomes than the PedsQL. Conclusions: The PedsQL was a well-accepted proposed primary outcome for children with hemorrhagic brain injuries. Traumatic intracranial hemorrhage progression was favored by a subset of clinicians. A plurality of participants also considered the PedsQL an acceptable outcome for children with hemorrhagic torso injuries. Blood product transfusion requirement was favored by fewer participants.
APA Citation
Nishijima, D., Gosdin, M., Naz, H., Tancredi, D., Hewes, H., Myers, S., Stanley, R., Adelson, P., Burd, R., Finkelstein, Y., VanBuren, J., Casper, T., & Kuppermann, N. (2020). Assessment of primary outcome measures for a clinical trial of pediatric hemorrhagic injuries. American Journal of Emergency Medicine, (). http://dx.doi.org/10.1016/j.ajem.2020.03.001