Highly efficient in vivo delivery of PMO into regenerating myotubes and rescue in laminin-α2 chain-null congenital muscular dystrophy mice.

Authors

Yoshitsugu Aoki
Tetsuya Nagata
Toshifumi Yokota
Akinori Nakamura
Matthew J A Wood
Terence Partridge, George Washington University
Shin'ichi Takeda

Document Type

Journal Article

Publication Date

12-15-2013

Journal

Human Molecular Genetics

Volume

22

Issue

24

Inclusive Pages

4914–4928

DOI

10.1093/hmg/ddt341

Keywords

Alternative Splicing; Animals; Base Sequence; Bromodeoxyuridine; Cardiotoxins; Cell Line; Cell Membrane Permeability; Disease Models, Animal; Dystrophin; Exons; Gene Expression; Gene Order; Humans; Laminin; Mice; Mice, Knockout; Morpholinos; Muscle Fibers, Skeletal; Muscular Dystrophies; Muscular Dystrophy, Animal; Muscular Dystrophy, Duchenne; Regeneration

APA Citation

Aoki, Y., Nagata, T., Yokota, T., Nakamura, A., Wood, M. J., Partridge, T., & Takeda, S. (2013). Highly efficient in vivo delivery of PMO into regenerating myotubes and rescue in laminin-α2 chain-null congenital muscular dystrophy mice.. Human Molecular Genetics, 22 (24). http://dx.doi.org/10.1093/hmg/ddt341

Peer Reviewed

1