"Highly efficient in vivo delivery of PMO into regenerating myotubes an" by Yoshitsugu Aoki, Tetsuya Nagata et al.
 

Highly efficient in vivo delivery of PMO into regenerating myotubes and rescue in laminin-α2 chain-null congenital muscular dystrophy mice.

Document Type

Journal Article

Publication Date

12-15-2013

Journal

Human Molecular Genetics

Volume

22

Issue

24

Inclusive Pages

4914–4928

DOI

10.1093/hmg/ddt341

Keywords

Alternative Splicing; Animals; Base Sequence; Bromodeoxyuridine; Cardiotoxins; Cell Line; Cell Membrane Permeability; Disease Models, Animal; Dystrophin; Exons; Gene Expression; Gene Order; Humans; Laminin; Mice; Mice, Knockout; Morpholinos; Muscle Fibers, Skeletal; Muscular Dystrophies; Muscular Dystrophy, Animal; Muscular Dystrophy, Duchenne; Regeneration

Peer Reviewed

1

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