Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study.

Authors

Eugenio Mercuri
Francesco Muntoni
Andrés Nascimento Osorio
Már Tulinius
Filippo Buccella
Lauren P. Morgenroth
Heather Gordish-Dressman, George Washington University
Joel Jiang
Panayiota Trifillis
Jin Zhu
Allan Kristensen
Claudio L. Santos
Erik K. Henricson
Craig M. McDonald
Isabelle Desguerre

Document Type

Journal Article

Publication Date

1-30-2020

Journal

Journal of Comparative Effectiveness Research

DOI

10.2217/cer-2019-0171

Comments

Epub ahead of print

APA Citation

Mercuri, E., Muntoni, F., Osorio, A. N., Tulinius, M., Buccella, F., Morgenroth, L. P., Gordish-Dressman, H., Jiang, J., Trifillis, P., Zhu, J., Kristensen, A., Santos, C. L., Henricson, E. K., McDonald, C. M., & Desguerre, I. (2020). Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study.. Journal of Comparative Effectiveness Research, (). http://dx.doi.org/10.2217/cer-2019-0171

Peer Reviewed

1