"Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotide" by Ugur Akpulat, Haicui Wang et al.
 

Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD.

Document Type

Journal Article

Publication Date

10-10-2018

Journal

Mol Ther Nucleic Acids

Volume

13

Inclusive Pages

534-542

DOI

10.1016/j.omtn.2018.10.002

Peer Reviewed

1

Open Access

1

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