"Oral cysteamine bitartrate and N-acetylcysteine for patients with infa" by Sondra Levin, Eva H. Baker et al.
 

Oral cysteamine bitartrate and N-acetylcysteine for patients with infantile neuronal ceroid lipofuscinosis: A pilot study

Document Type

Response or Comment

Publication Date

8-2014

Journal

Lancet Neurology

Volume

Volume 13, Issue 8

Inclusive Pages

777-787

DOI

10.1016/S1474-4422(14)70142-5

Keywords

Acetylcysteine--administration & dosage; Cysteamine--administration & dosage; Neuronal Ceroid-Lipofuscinoses--diagnosis; Neuronal Ceroid-Lipofuscinoses--drug therapy

Comments

Comment in

Development of new treatments for Batten disease. [Lancet Neurol. 2014]

Peer Reviewed

1

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