An immune tolerance approach using transient low-dose methotrexate in the ERT-naïve setting of patients treated with a therapeutic protein: experience in infantile-onset Pompe disease.

Authors

Zoheb B Kazi
Ankit K Desai
R Bradley Troxler
David Kronn
Seymour Packman
Marta Sabbadini
William B Rizzo
Katalin Scherer
Omar Abdul-Rahman
Pranoot Tanpaiboon, George Washington University
Sheela Nampoothiri
Neerja Gupta
Annette Feigenbaum
Dmitriy M Niyazov
Langston Sherry
Reeval Segel
Alison McVie-Wylie
Crystal Sung
Alexandra M Joseph
Susan Richards
Priya S Kishnani

Document Type

Journal Article

Publication Date

9-14-2018

Journal

Genetics in medicine : official journal of the American College of Medical Genetics

DOI

10.1038/s41436-018-0270-7

Comments

epub ahead of print

APA Citation

Kazi, Z., Desai, A., Troxler, R., Kronn, D., Packman, S., Sabbadini, M., Rizzo, W., Scherer, K., Abdul-Rahman, O., Tanpaiboon, P., Nampoothiri, S., Gupta, N., Feigenbaum, A., Niyazov, D., Sherry, L., Segel, R., McVie-Wylie, A., Sung, C., Joseph, A., Richards, S., & Kishnani, P. (2018). An immune tolerance approach using transient low-dose methotrexate in the ERT-naïve setting of patients treated with a therapeutic protein: experience in infantile-onset Pompe disease.. Genetics in medicine : official journal of the American College of Medical Genetics, (). http://dx.doi.org/10.1038/s41436-018-0270-7

Peer Reviewed

1