Bodywide skipping of exons 45-55 in dystrophic mdx52 mice by systemic antisense delivery.

Authors

Yoshitsugu Aoki, National Center of Neurology and Psychiatry, Kodaira, Tokyo, Japan
Toshifumi Yokota, Children's National Medical Center
Tetsuya Nagata, National Center of Neurology and Psychiatry, Kodaira, Tokyo, Japan
Akinori Nakamura, Shinshu University School of Medicine, Matsumoto, Japan
Jun Tanihata, National Center of Neurology and Psychiatry, Kodaira, Tokyo, Japan
Takashi Saito, Tokyo Women's Medical University, Shinjuku, Tokyo, Japan
Stephanie Duguez, Children's National Medical Center
Kanneboyina Nagaraju, George Washington University
Eric P. Hoffman, George Washington UniversityFollow
Terence Partridge, Children's National Medical CenterFollow
Shin'ichi Takeda, National Center of Neurology and Psychiatry, Kodaira, Tokyo, Japan

Document Type

Journal Article

Publication Date

8-21-2012

Journal

Proceedings of the National Academy of Sciences of the United States of America

Volume

Volume 109 Issue, 34

Inclusive Pages

13763-13768

Keywords

Dystrophin--genetics; Exons; Genetic Therapy--methods; Muscular Dystrophy; Duchenne--genetics; Oligonucleotides; Antisense--genetics

Comments

This is an open access PubMed Central article. Click on link for full-text access.

APA Citation

Aoki, Y., Yokota, T., Nagata, T., Nakamura, A., Tanihata, J., Saito, T., . . . Takeda, S. (2012). Bodywide skipping of exons 45-55 in dystrophic mdx52 mice by systemic antisense delivery. Proceedings of the National Academy of Sciences of the United States of America, 109(34), 13763-13768.

Peer Reviewed

1

Open Access

1