Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD.

Ugur Akpulat
Haicui Wang
Kerstin Becker
Adriana Contreras
Terence A Partridge, George Washington University
James S Novak, George Washington University
Sebahattin Cirak

Abstract