The cooperative international neuromuscular research group Duchenne natural history study: Glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures

Authors

Erik K. Henricson, University of California - Davis
R. Ted Abresch, University of California - Davis
Avital Cnaan, George Washington UniversityFollow
Fengming Hu, Children's National Medical Center, Washington, DC
Tina Duong, Children's National Medical Center, Washington, DC
Adrienne Arrieta, Children's National Medical Center, Washington, DC
Jay Han, University of California - Davis
Diana M. Escolar, Kennedy Krieger Institute, Baltimore, MD
Julaine M. Florence, Washington University in St Louis
Paula R. Clemens, University of Pittsburgh
Eric P. Hoffman, George Washington UniversityFollow
Craig M. McDonald, University of California - Davis
CINRG Investigators

Document Type

Journal Article

Publication Date

2013

Journal

Muscle and Nerve

Volume

Volume 48, Issue 1

Inclusive Pages

55-67

Keywords

Disease Progression; Glucocorticoids--therapeutic use; International Cooperation; Muscular Dystrophy; Duchenne--drug therapy; Outcome Assessment (Health Care)--methods

APA Citation

Henricson, E. K., Abresch, R. T., Cnaan, A., Hu, F., Duong, T., Arrieta, A., Han, J., Escolar, D.M., Florence, J.M., Clemens, P.R., Hoffman, E.P., Mcdonald, C. M. (2013). The cooperative international neuromuscular research group duchenne natural history study: Glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures. Muscle and Nerve, 48(1), 55-67.

Peer Reviewed

1