Title

Orphan drug development in muscular dystrophy: Update on two large clinical trials of dystrophin rescue therapies

Document Type

Journal Article

Publication Date

11-2013

Journal

Discovery Medicine

Volume

Volume 16, Issue 89

Inclusive Pages

233-239

Keywords

Dystrophin--metabolism; Muscular Dystrophies--drug therapy; Muscular Dystrophies--metabolism; Orphan Drug Production

Comments

This is an open access article. Click on link for full-text access.

Peer Reviewed

1

Open Access

1