Title

A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice.

Document Type

Journal Article

Publication Date

3-1-2016

Journal

Nature Biotechnology

Volume

34

Issue

3

Inclusive Pages

334-338

DOI

10.1038/nbt.3469

Keywords

CRISPR-Cas Systems--genetics; Ornithine Carbamoyltransferase--genetics; Ornithine Carbamoyltransferase Deficiency Disease--therapy; RNA Editing

Comments

This is an open access PubMed Central article. Click on link for full-text access.

Peer Reviewed

1

Open Access

1